A Phase 1/2, Open-Label, Single-Dose, Multicenter Study to Evaluate the Pharmacokinetics and Safety of Human Plasma-...
Introduction Severe congenital protein C deficiency (SCPCD) is a rare autosomal recessive disorder arising from homozygous or compound heterozygous variants in the protein C gene (PROC).1 These result in low or undetectable levels of protein C activity, …