Optimizing Care in Patients with Paroxysmal Nocturnal Hemoglobinuria: Managing Suboptimal Response and Uncontrolled ...
Introduction Complement inhibitor treatment has revolutionized the care of patients with paroxysmal nocturnal hemoglobinuria (PNH). Historically, the 10-year mortality rate with best supportive treatment was approximately 35%.1 Survival rates have, however …