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Published on 03:43 GMT

Health Secretary Neil Gray facing fury over failure to deliver muscular dystrophy drug

Health Secretary Neil Gray has been furiously condemned for failing to ensure access to a new muscular dystrophy drug for desperate children. About 30 boys with a rare form of the killer disease could have their lives extended by givinostat. It slows …

Source: Daily Record & Sunday Mail - Left-wing
Published on May 9, 2025

'It was eye-opening': How a WoW documentary inspired Muscular Dystrophy UK's Liam Quinn to raise money and build ...

I had the pleasure of attending a Netflix event around the WoW documentary The Remarkable Life of Ibelin last year—one that was attended by folks from Muscular Dystrophy UK, a charity that helps fund research into the kinds of muscle-wasting conditions …

Source: PC Gamer - Neutral
Published on May 10, 2025

FDA States Advisory Committee Meeting Will be Held for Capricor’s BLA for DMD Cardiomyopathy Cell Therapy Deramiocel

In a mid-cycle review meeting between the FDA and Capricor Therapeutics regarding the latter’s biologics license application (BLA) for Deramiocel (also known as CAP-1002), an investigational allogeneic cardiosphere-derived cell therapy intended to treat …

Source: CGTLive - Neutral
Published on May 9, 2025

Science is rewriting the Duchenne muscular dystrophy lifespan

Duchenne muscular dystrophy (DMD) is the most common muscular dystrophy, affecting 1 in 3500-6000 boys. It is caused by changes in the dystrophin gene, located on the X chromosome, which results in progressive muscle weakness. Boys with DMD typically …

Source: Monash University Lens - Left-wing
Published on May 9, 2025

Access to funds and affordable treatments remain key challenges in Duchenne Muscular Dystrophy care in India

Duchenne muscular dystrophy (DMD), recognised by the World Health Organization (WHO) as a rare disease, is the most common form of childhood muscular dystrophy. It is a progressive genetic disorder that primarily affects boys, leading to gradual muscle …

Source: The Hindu - Center-left
Published on May 8, 2025

ASGCT 2025: CRISPR-Cas12 Editing Shows Early Clinical Benefit in Duchenne Muscular Dystrophy

At the upcoming annual meeting of the American Society of Cell and Gene Therapy, scientists from Huidagene Therapeutics will share an update on the development of their CRISPR-high-fidelity(hf)Cas12Max-based gene editing therapy for Duchenne muscular …

Source: Genetic Engineering & Biotechnology News -New York - Pending
Published on May 9, 2025

New FDA Leadership Could Raise The Bar For Drug Approvals

Introduction New FDA Leadership Team: The FDA's top leadership has shifted under Commissioner Dr. Marty Makary, with Dr. Vinayak "Vinay" Prasad now heading the Center for Biologics Evaluation and Research (CBER) and Dr. Sanjula Jain-Nagpal …

Source: Benzinga - Neutral
Published on May 9, 2025

Catalyst Pharmaceuticals, Inc. (NASDAQ:CPRX) Q1 2025 Earnings Call Transcript

Catalyst Pharmaceuticals, Inc. (NASDAQ:CPRX) Q1 2025 Earnings Call Transcript May 8, 2025 Operator: Good day everyone, and welcome to the Catalyst Pharmaceuticals First Quarter 2025 Financial Results Conference Call. At this time, all participants are in a …

Source: Insider Monkey - Neutral
Published on May 9, 2025

Capricor’s DMD Cardiomyopathy Therapy to Face FDA Advisory Committee

The maker of an investigational cell therapy for Duchenne muscular dystrophy (DMD) says its lead product will go before an FDA advisory committee in advance of an expected late-summer approval decision from the agency. Capricor Therapeutics says it does …

Source: Managed Healthcare Executive - Neutral
Published on May 8, 2025

FDA Fast-Tracks Givinostat for Polycythemia Vera Treatment

The FDA has granted givinostat (Duvyzat) fast track status for the treatment of patients with polycythemia vera (PV). Givinostat is an orally administered histone deacetylase (HDAC) inhibitor. The agent is currently being assessed in the ongoing phase 3 …

Source: Targeted Oncology - Pending
Published on 01:18 GMT

Hong Kong teen expected to die soon has heartfelt Mother’s Day message for mum

On Sunday, Michelle Li Yuan-feng knew it was possibly one of her last Mother’s Day celebrations with her teenage son, Chen Tsz-kin, who planned to treat her to classic Cantonese charcoal-roasted goose for lunch. Tsz-kin said it was his way of thanking his …

Source: South China Morning Post - Indeterminate
Published on May 10, 2025

EAP Program Authorized for ALS Agent SPG302, PTC518 Meets Primary End Point, Capricor Completes Mid-Cycle Review for ...

WATCH TIME: 4 minutes Welcome to this special edition of Neurology News Network. I'm Marco Meglio. According to a new announcement, the FDA has authorized Spinogenix’s expanded access program (EAP) for its investigational amyotrophic lateral sclerosis …

Source: NeurologyLive - Neutral
Published on May 8, 2025

Biotech is guessing how Vinay Prasad might change the FDA. His research, writing offer clues.

To hear Vinay Prasad tell it, U.S. healthcare is too ready to intervene unnecessarily, use prescription drugs without sufficient evidence of their benefit and put patients at risk of side effects or other negative outcomes. The Food and Drug Administration …

Source: BioPharma Dive - Pending
Published on May 8, 2025

Trump’s diversity purge freezes hundreds of millions in medical research at universities across the country

(CNN) — Universities across the country are scrambling to comply with President Donald Trump’s anti-diversity push in an effort to hold on to hundreds of millions of dollars in federal grants that fund critical medical research in areas such as cancer and …

Source: Crossroads Today - Texas - Neutral
Published on May 8, 2025

Biotech Stocks Slide After FDA Selects Prasad to Lead CBER

The FDA’s Center for Biologics Evaluation and Research (CBER) will have a new director, as Vinay Prasad, MD, MPH, will fill the role following the resignation of Peter Marks, MD, PhD, 5 weeks ago.1 The leadership change was reported widely on Tuesday, …

Source: The American Journal of Managed Care - Neutral
Published on May 8, 2025

Vinay Prasad’s FDA Appointment ‘Anything But Status Quo’

Vinay Prasad is an oncologist and hematologist at the University of California, San Francisco, as well as a frequent health policy critic on his YouTube channel and various podcasts. Now, he can add chief of the FDA’s Center for Biologics Evaluation and …

Source: BioSpace - Pending
Published on May 5, 2025

STAT+: FDA will ask outside experts to review Capricor’s therapy for Duchenne muscular dystrophy

Want to stay on top of the science and politics driving biotech today? Sign up to get our biotech newsletter in your inbox. Today, we explore how an ambitious nonprofit is taking control of a shelved gene therapy, as it seeks to create a new model for …

Source: STAT - Massachusetts - Neutral
Published on May 7, 2025

Sarepta tries to quell concerns over DMD gene therapy Elevidys as patients delay treatment after death report

Sarepta Therapeutics CEO Doug Ingram opened the company’s first-quarter earnings call Tuesday by acknowledging that, like the broader biopharma industry, the genetic medicine biotech is facing a challenging time. Following report of a patient’s death after …

Source: Fierce Pharma - Neutral
Published on May 7, 2025

Sarepta shares plummet as lower sales outlook adds to gloom over FDA’s new biologics hire

Dive Brief: Sarepta Therapeutics shares slid 19% early Wednesday after the biotechnology company lowered its sales forecast for the year on the heels of a slower-than-expected first quarter for its top-selling product. Full-year product revenue will likely …

Source: BioPharma Dive - Pending

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Published on May 10, 2025 - 13:10 GMT

Healthcare Digital Twins Market Size to Hit USD 6.80 Billion by 2032, growing at 25.7% CAGR, says Coherent Market ...

Burlingame, CA, May 10, 2025 (GLOBE NEWSWIRE) -- According to Coherent Market Insights, the global healthcare digital twins market size was evaluated at USD 1.37 Bn in 2025 and is estimated to attain USD 6.80 Bn by 2032, growing at a CAGR of 25.7% during …

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Published on May 9, 2025 - 23:36 GMT

RPM Healthcare Study on Stage 2 Hypertension Published in The American Journal of Managed Care

ST. PETERSBURG, FL, FL, UNITED STATES, May 9, 2025 /⁨EINPresswire.com⁩/ -- RPM Healthcare is proud to announce the publication of its peer-reviewed study, “Effect of Remote Patient Monitoring on Stage 2 Hypertension,” in The American Journal of …

Distribution channels: Companies, Healthcare & Pharmaceuticals Industry ...

Published on May 9, 2025 - 23:36 GMT

RPM Healthcare Applauds New York’s Medicaid Reimbursement for Remote Patient Monitoring

ST. PETERSBURG, FL, UNITED STATES, May 9, 2025 /⁨EINPresswire.com⁩/ -- RPM Healthcare proudly supports New York State Medicaid’s decision to reimburse Remote Patient Monitoring (RPM) services under CPT code 99457, marking a significant advancement …

Distribution channels: Companies, Healthcare & Pharmaceuticals Industry ...
Published on May 10, 2025 - 03:46 GMT

AHA expresses support for Save Healthcare Workers Act

The AHA May 8 voiced support for the Save Healthcare Workers Act to House and Senate sponsors of the legislation. The bipartisan bill would make it a federal crime to assault hospital workers, similar to current federal law protecting airline and airport …

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Published on May 9, 2025 - 23:59 GMT

Gov. Kemp Signs FY26 Budget - Providing Hurricane Helene Relief and Important Investments in Education, Healthcare, and ...

ATLANTA, GEORGIA, May 9 - Governor Brian P. Kemp, joined by First Lady Marty Kemp, Lt. Governor Burt Jones, House Appropriations Chairman Hatchett, constitutional officers, and members of the Georgia General Assembly, and state leaders today signed the …

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Published on May 9, 2025 - 10:23 GMT

U.S. Home Healthcare Market Set to Witness Significant Growth by 2025-2032 | Medline Industries Inc., Medtronic Plc, 3M

BURLINGAME, CA, UNITED STATES, May 9, 2025 /⁨EINPresswire.com⁩/ -- U.S. Home Healthcare Market is estimated to be valued at USD 26.59 Bn in 2025 and is expected to reach USD 40.78 Bn in 2032, exhibiting a compound annual growth rate (CAGR) of 6. …

Distribution channels: Healthcare & Pharmaceuticals Industry
Published on May 9, 2025 - 10:13 GMT

Rfid In Healthcare Market Projected To Witness Massive Growth, 2025-2032 | Microchip Technology, Accenture, Hitachi, 3M

BURLINGAME, CA, UNITED STATES, May 9, 2025 /⁨EINPresswire.com⁩/ -- Rfid In Healthcare Market is estimated to be valued at USD 11.9 Bn in 2025 and is expected to reach USD 43.39 Bn in 2032, exhibiting a compound annual growth rate (CAGR) of 20.3% from …

Distribution channels: Healthcare & Pharmaceuticals Industry
Published on May 9, 2025 - 21:02 GMT

HOW DO U.S. HEALTHCARE PROVIDERS KNOW HOW AND WHERE TO SELL $3.4B ANNUALLY IN SERVICES TO INTERNATIONAL CLIENTS?

Medical centers and other U.S. providers of high-acuity or highly specialized healthcare services offer care that is unsurpassed in the world. Prior to 2010, no one really knew how well this industry was doing in international markets. That’s when, through …

Distribution channels: Business & Economy

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Published on May 11, 2025 - 10:53 GMT

Best Skin Tag Remover 2025: Revitag Review & Top Skin Tag Removal Tips

Tallmadge, OH, May 11, 2025 (GLOBE NEWSWIRE) -- Introduction Skin tags—small, benign growths on the skin—can be a nuisance for many people. Though harmless, these soft, hanging pieces of skin often appear on the neck, underarms, eyelids, or other areas …

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Published on May 10, 2025 - 20:00 GMT

First 5 California and First 5 San Diego Announce Stronger Starts Statewide Day of Action with Family Event

First 5 California and First 5 San Diego hosted a joint event today to commemorate Stronger Starts Statewide Day of Action 2025 SAN DIEGO, CA, UNITED STATES, May 10, 2025 /⁨EINPresswire.com⁩/ -- First 5 California and First 5 San Diego hosted a joint …

Distribution channels: Education, Healthcare & Pharmaceuticals Industry ...
Published on May 10, 2025 - 17:57 GMT

California Dispensaries Redefine Cannabis Retail Through Innovation and Community Engagement

818 Brands, Gradus Hollywood, and The Syndicate Tarzana Showcase Distinctive Approaches to Customer Experience and Local Connection LOS ANGELES, CA, UNITED STATES, May 10, 2025 /⁨EINPresswire.com⁩/ -- As California’s cannabis industry continues to …

Distribution channels: Consumer Goods, Culture, Society & Lifestyle ...
Published on May 10, 2025 - 17:26 GMT

Charitable Intentions Inspire Charitable Results at REVEL

REVEL’S Charity Carnaval in 2025 Will Support SickKids Foundation NIAGARA FALLS, ONTARIO, CANADA, May 10, 2025 /⁨EINPresswire.com⁩/ -- The REVEL Charity Carnaval has become a unique, annual tradition, hosted by REVEL REALTY INC. in support of …

Distribution channels: Banking, Finance & Investment Industry, Companies ...
Published on May 10, 2025 - 17:13 GMT

Chronicle Associates Presents: Pursuit of Freedom – A Memoir of Courage and Reinvention

Chronicle Associates Presents: From Tehran to Triumph: Fariba Kalantari’s Inspiring Memoir “Pursuit of Freedom” Chronicles the Journey of Reinvention and Hope HOUSTON, TX, UNITED STATES, May 10, 2025 /⁨EINPresswire.com⁩/ -- Pursuit of Freedom: A …

Distribution channels: Book Publishing Industry, Business & Economy ...
Published on May 10, 2025 - 16:41 GMT

Surgeon General's Warning: Social Media Risks Demand Comprehensive Youth Mental Health Support

U.S. Surgeon General warns of social media’s harm to youth mental health, urging action to curb risks like anxiety, depression, and cyberbullying. CA, UNITED STATES, May 10, 2025 /⁨EINPresswire.com⁩/ -- The U.S. Surgeon General’s Advisory on …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on May 10, 2025 - 16:00 GMT

The Role of Hair Transplantation in Boosting Self-Esteem and Confidence – Smile Hair Clinic's Expertise

ISTANBUL, TURKEY, May 10, 2025 /⁨EINPresswire.com⁩/ -- Hair loss is a common issue that affects millions of people worldwide, and its impact goes beyond just physical appearance. It can significantly affect one’s self-esteem and confidence, leading …

Distribution channels: Beauty & Hair Care, Healthcare & Pharmaceuticals Industry ...
Published on May 10, 2025 - 18:25 GMT

Best Vyvanse Alternative Over the Counter for ADHD - Natural Vyvanse Substitute - Noocube

London, May 10, 2025 (GLOBE NEWSWIRE) -- Vyvanse is a prescription medication that is used to treat ADHD symptoms, but it can be expensive and some people don't like the idea of taking a drug class medicine or stimulant medications. For these reasons …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on May 10, 2025 - 16:28 GMT

Akero Therapeutics présente les résultats de la 96e semaine de l’essai clinique de phase 2b SYMMETRY sur l’éfruxifermine ...

SOUTH SAN FRANCISCO, État de Californie, 10 mai 2025 (GLOBE NEWSWIRE) -- Akero Therapeutics, Inc. (NASDAQ : AKRO), une société en phase clinique développant des traitements révolutionnaires pour les patients atteints de maladies métaboliques graves et dont …

Distribution channels: Culture, Society & Lifestyle, Healthcare & Pharmaceuticals Industry ...
Published on May 10, 2025 - 16:28 GMT

Akero Therapeutics präsentiert auf dem EASL-Kongress 2025 die Ergebnisse nach 96 Wochen der klinischen Phase-IIb-Studie ...

SOUTH SAN FRANCISCO, Kalifornien, May 10, 2025 (GLOBE NEWSWIRE) -- Akero Therapeutics, Inc. (Nasdaq: AKRO), ein in der klinischen Phase tätiges Unternehmen, das bahnbrechende Therapien für Patienten mit schwerwiegenden Stoffwechselkrankheiten entwickelt, …

Distribution channels: Culture, Society & Lifestyle, Healthcare & Pharmaceuticals Industry ...
Published on May 10, 2025 - 15:03 GMT

MEDVi Under Review: Best GLP-1 Semaglutide & Terzepatide Compound Solution for Personalized Weight Loss

New York, May 10, 2025 (GLOBE NEWSWIRE) -- In This Article, You’ll Discover: The growing challenges with traditional weight loss methods and why most diets fail What GLP-1 receptor agonists like Semaglutide and Tirzepatide are and how they support …

Distribution channels: Healthcare & Pharmaceuticals Industry, Media, Advertising & PR ...
Published on May 10, 2025 - 12:21 GMT

Sumatra Slim Belly Tonic Reviews: 2025 Real User Reviews Analyzed & Verified (Blue Tonic for Weight Loss)

LOS ANGELES, May 10, 2025 (GLOBE NEWSWIRE) -- Losing weight these days can feel more difficult than ever. Despite trying countless diets, workout routines, and the latest supplements, many people still struggle with stubborn belly fat that just won't …

Distribution channels: Healthcare & Pharmaceuticals Industry, Media, Advertising & PR ...
Published on May 9, 2025 - 23:36 GMT

RPM Healthcare Applauds New York’s Medicaid Reimbursement for Remote Patient Monitoring

ST. PETERSBURG, FL, UNITED STATES, May 9, 2025 /⁨EINPresswire.com⁩/ -- RPM Healthcare proudly supports New York State Medicaid’s decision to reimburse Remote Patient Monitoring (RPM) services under CPT code 99457, marking a significant advancement …

Distribution channels: Companies, Healthcare & Pharmaceuticals Industry ...
Published on May 9, 2025 - 23:36 GMT

RPM Healthcare Study on Stage 2 Hypertension Published in The American Journal of Managed Care

ST. PETERSBURG, FL, FL, UNITED STATES, May 9, 2025 /⁨EINPresswire.com⁩/ -- RPM Healthcare is proud to announce the publication of its peer-reviewed study, “Effect of Remote Patient Monitoring on Stage 2 Hypertension,” in The American Journal of …

Distribution channels: Companies, Healthcare & Pharmaceuticals Industry ...
Published on May 10, 2025 - 11:15 GMT

Madrigal Announces New Clinical Data Demonstrating Rezdiffra™ (resmetirom) Significantly Improved Multiple Noninvasive ...

Late-breaking results from the open-label compensated MASH cirrhosis (F4c) arm of the Phase 3 MAESTRO-NAFLD-1 trial presented at the EASL Congress 65% of patients with clinically significant portal hypertension (CSPH) at baseline moved into lower risk …

Distribution channels: Healthcare & Pharmaceuticals Industry, Media, Advertising & PR ...
Published on May 9, 2025 - 22:56 GMT

Nurses Denounce Trump Health Policies to Celebrate Nurses Week

Nursing advocates release statement and video calling for global resistance to Trump Administration’s attacks on public health BALTIMORE, MD, UNITED STATES, May 9, 2025 /⁨EINPresswire.com⁩/ -- Hundreds of nurses have signed a statement opposing …

Distribution channels: Environment, Healthcare & Pharmaceuticals Industry ...
Published on May 9, 2025 - 22:50 GMT

Less Cancer Calls on Congress to Exercise Compassion as DOGE Cuts Cancer Research and Prevention Initiatives

WASHINGTON, DC, UNITED STATES, May 9, 2025 /⁨EINPresswire.com⁩/ -- Less Cancer, a 501(c)3 charity working to educate the public and create proactive public policies regarding cancer and cancer prevention, is calling on Congress and the public to …

Distribution channels: Companies, Culture, Society & Lifestyle ...
Published on May 10, 2025 - 10:08 GMT

6 Best Fat Burners For Women: Top Over the Counter and Online Pills and Fat Burning Supplements For Women Weight Loss In ...

New York City, NY, May 10, 2025 (GLOBE NEWSWIRE) -- It has now been proven scientifically that women may have a harder time losing weight and burning off body fat as compared to men. Doesn’t seem fair, but this is the truth. Why this happens is because of …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on May 10, 2025 - 09:14 GMT

Best Fat Burners For Men 2025: Top Weight Loss Pills & Supplements For Fast Fat Loss - Wolfson Brands Ltd

New York City, May 10, 2025 (GLOBE NEWSWIRE) -- Introduction: Why Fat Burners Are a Game-Changer for Men in 2025 Losing weight and building a leaner physique are common goals for men in 2025. But even with the best diet and workout routine, shedding …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on May 10, 2025 - 09:10 GMT

4 Best Supplements for Muscle Growth in 2025 - Legal Steroid Alternatives & Bodybuilding Supplements for Bulking and ...

Glasgow, May 10, 2025 (GLOBE NEWSWIRE) -- The best legal supplements for muscle growth is presented by Wolfson Brands Building serious muscle isn’t just about hitting the gym hard, it’s about giving your body the right supplements to gain muscle size, …

Distribution channels: Healthcare & Pharmaceuticals Industry ...