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Published on Mar 31, 2025

Pep-Therapy advancing orphan drug PEP-010 in pancreatic cancer

French biotech Pep-Therapy SAS is in the midst of raising a €20 million (US$21.62 million) round and, at the same time, prospecting for potential partners after winning FDA orphan drug designation for its bifunctional peptide Pep-010 in the treatment of …

Source: BioWorld - Label Pending
Published on Mar 31, 2025

FDA Grants BA1302 Orphan Drug Designation for Squamous NSCLC and Pancreatic Cancer

The FDA granted an orphan drug designation to BA1302 (Boan Biotechnology) for the treatment of patients with squamous non-small cell lung cancer (NSCLC) and pancreatic cancer.1 Preclinical studies have demonstrated BA1302’s potent internalization and …

Source: Pharmacy Times - Neutral
Published on Mar 31, 2025

Orphan drugs will double their market share by 2030

Once specialized treatments for rare conditions, orphan drugs are now challenging the dominance of mainstream medications. Highlighted in two Evaluate reports, "Are Orphans That Different?" and "Top Orphan Drugs: Still a Class Apart?", …

Source: mHealthIntelligence - Neutral
Published on Apr 1, 2025

First Patient Dosed With Annamycin and Cytarabine in Phase 3 AML Trial

The first patient with relapsed or refractory acute myeloid leukemia, or AML, has been dosed with annamycin in combination with cytarabine (also known as “Ara-C”) in the global phase 3 MIRACLE trial, according to a press release from Moleculin Biotech, Inc …

Source: Cure Today - Neutral
Published on Apr 1, 2025

Yingli Pharma Announces Successful End-of-Phase 2 Meeting with FDA and Clearance of Global Multi-center Phase 3 ...

SAN FRANCISCO, April 1, 2025 /PRNewswire/ — Shanghai Yingli Pharmaceutical Co., Ltd. (Yingli Pharma), a clinical stage biotechnology company developing oral small molecule drugs for cancer, metabolic, and immune diseases, announced today that it …

Source: The Laotian Times - Uncategorized
Published on Apr 1, 2025

Monoclonal Antibody Bentracimab Shown to Reverse Antiplatelet Effect of Brilinta | ACC 2025

Bentracimab, a monoclonal antibody administered intravenously, can be an effective agent to quickly reverse the effects of the antiplatelet agent Brilinta (ticagrelor) in patients who need to have urgent surgery or who are having major bleeding, a study …

Source: Managed Healthcare Executive - Neutral
Published on Apr 1, 2025

FDA Approves fitusiran for Hemophilia A and B

The FDA has approved fitusiran, now named Qfitlia, for routine prophylaxis in patients aged 12 and older with hemophilia A or B, with or without inhibitors. Qfitlia offers less frequent administration, improving the patient experience. Its approval was …

Source: Medical Dialogues - Uncategorized
Published on 02:27 GMT

Reducing Polycythemia Vera–Associated Thrombotic Risk Through Iron Regulation

The investigational rusfertide (Takeda), is currently being evaluated in the phase 3 VERIFY trial (NCT05210790) as an injectable therapeutic to treat polycythemia vera (PV) through achieving and sustaining hematocrit control. This agent has already …

Source: The American Journal of Managed Care - Neutral
Published on Apr 1, 2025

Therapeutic Potential of Silmitasertib Observed in Huntington Disease Mouse Model

Newly presented preclinical research suggests that silmitasertib (CX4945), an FDA-designated orphan drug for cancer, may offer therapeutic benefits for Huntington disease (HD) by reducing mutant huntingtin (mHTT) aggregation and improving motor function in …

Source: NeurologyLive - Label Pending
Published on Apr 1, 2025

FDA news in pedatrics: March 2025

Another month has come and gone, and with it, several FDA approvals and regulatory updates related to the ever-evolving landscape of pediatric health care. In our March monthly recap, we list our top FDA-related news items so you can stay informed in an …

Source: Contemporary Pediatrics - Neutral
Published on Mar 29, 2025

Henlius Receives Orphan-Drug Designation for HLX22 (anti-HER2 mAb) for Gastric Cancer

On March 19, 2025, Shanghai Henlius Biotech announced that the FDA has granted Orphan Drug Designation for HLX22, an anti-HER2 monoclonal antibody, for the treatment of gastric cancer. HLX22 binds to HER2 extracellular subdomain IV at a different binding …

Source: JD Supra - California - Neutral
Published on Apr 1, 2025

Corcept’s Phase III trial of ovarian cancer therapy shows PFS improvement

Corcept Therapeutics’ pivotal Phase III ROSELLA trial of oral relacorilant in combination with nab-paclitaxel has met its primary endpoint, demonstrating an improvement in progression-free survival (PFS) in individuals with platinum-resistant ovarian …

Source: Clinical Trials Arena - Label Pending
Published on Apr 1, 2025

Investornewsbreaks CNS Pharmaceuticals Inc. (NASDAQ: CNSP) Advances TPI 287 For GBM, Ends 2024 With Strong Cash ...

(MENAFN- Investor Brand Network) CNS Pharmaceuticals (NASDAQ: CNSP) a biopharmaceutical company targeting brain and CNS cancers, reported a full-year 2024 net loss of $14.9 million, down from $18.9 million in 2023, due to reduced R&D spending. Despite …

Source: MENAFN - Uncategorized
Published on Mar 27, 2025

Crinetics Pharmaceuticals Announces European Medicines Agency (EMA) Validation of Marketing Authorization Application (...

SAN DIEGO, March 27, 2025 (GLOBE NEWSWIRE) -- Crinetics Pharmaceuticals, Inc. (Nasdaq: CRNX) today announced that the European Medicines Agency (EMA) has validated the Marketing Authorization Application (MAA) for paltusotine, the first once-daily, oral, …

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Published on Apr 1, 2025

Moleculin Doses First Patient in Pivotal, Adaptive Phase 3 MIRACLE Trial

– Initial data readout on track for second half of 2025 HOUSTON, April 01, 2025 (GLOBE NEWSWIRE) -- Moleculin Biotech, Inc., (Nasdaq: MBRX) (“Moleculin” or the “Company”), a late-stage pharmaceutical company with a broad portfolio of drug candidates …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on Apr 1, 2025

Medera Presented Updated Results from First-In-Human Gene Therapy Trial for Heart Failure with Preserved Ejection ...

BOSTON, April 01, 2025 (GLOBE NEWSWIRE) -- Medera Inc. (“Medera”), a clinical-stage biopharmaceutical company focused on targeting cardiovascular diseases by developing a range of next-generation therapeutics, today announced that updated results from its …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on Apr 1, 2025

Candel Therapeutics Announces Publication of Phase 1b Clinical Trial Data on the Combination of CAN-2409 and Nivolumab ...

NEEDHAM, Mass., April 01, 2025 (GLOBE NEWSWIRE) -- Candel Therapeutics, Inc. (Candel or the Company) (Nasdaq: CADL), a clinical stage biopharmaceutical company focused on developing multimodal biological immunotherapies to help patients fight cancer, today …

Distribution channels: Healthcare & Pharmaceuticals Industry, Technology ...
Published on Apr 1, 2025

Revive Therapeutics Announces Acquisition of Molecular Hydrogen Program

TORONTO, April 01, 2025 (GLOBE NEWSWIRE) -- Revive Therapeutics Ltd. (“Revive” or the “Company”) (OTCQB: RVVTF) (CSE: RVV) (FRANKFURT:31R), a specialty life sciences company focused on the research and development of therapeutics for infectious diseases, …

Distribution channels: Companies, Technology ...
Published on Apr 1, 2025

Pharvaris Announces Orphan Designation Granted to Deucrictibant by the European Commission

ZUG, Switzerland, April 01, 2025 (GLOBE NEWSWIRE) -- Pharvaris (Nasdaq: PHVS), a late-stage biopharmaceutical company developing novel, oral bradykinin B2 receptor antagonists to help address unmet needs of those living with bradykinin-mediated diseases …

Distribution channels: Healthcare & Pharmaceuticals Industry, Media, Advertising & PR ...

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Published on April 1, 2025 - 16:59 GMT

Meeting the Growing Demand for Executive Healthcare in Toronto

Efficient healthcare in Toronto meets the needs of busy individuals with personalized, proactive solutions. TORONTO, ON, CANADA, April 1, 2025 /⁨EINPresswire.com⁩/ -- Balancing work, family, and personal well-being can be challenging, particularly …

Distribution channels: Beauty & Hair Care, Business & Economy ...
Published on April 1, 2025 - 13:00 GMT

Courtemanche & Associates Introduces Transition Services to Help Healthcare Organizations Navigate Accreditation Changes

Comprehensive support ensures compliance with evolving regulatory standards and strengthens healthcare quality and patient safety. CHARLOTTE, NC, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- With healthcare regulations constantly evolving, …

Distribution channels: Healthcare & Pharmaceuticals Industry ...

Published on April 2, 2025 - 00:22 GMT

Caretaker Medical Receives Inaugural Healthcare Tech Innovation Award and $200,000 Grant from Medical Society of D.C.

WASHINGTON, DC, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- Caretaker Medical is honored to announce it has been awarded the Healthcare Technology Innovation Award, along with a $200,000 grant, from the Medical Society of the District of …

Distribution channels: Banking, Finance & Investment Industry, Emergency Services ...
Published on April 1, 2025 - 23:09 GMT

Malasakit Center eases hospital expenses for poor Quezon City residents as Bong Go pushes for continuous healthcare ...

PHILIPPINES, April 1 - Press Release March 31, 2025 Malasakit Center eases hospital expenses for poor Quezon City residents as Bong Go pushes for continuous healthcare access for all Arnold Daniel, 47, from Payatas, Quezon City, was hospitalized at East …

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Published on April 1, 2025 - 20:05 GMT

Cidara Therapeutics to Participate in the 24th Annual Needham Virtual Healthcare Conference

SAN DIEGO, April 01, 2025 (GLOBE NEWSWIRE) -- Cidara Therapeutics, Inc. (Nasdaq: CDTX), a biotechnology company using its proprietary Cloudbreak® platform to develop drug-Fc conjugate (DFC) immunotherapies, today announced that company management will …

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Published on April 1, 2025 - 19:20 GMT

LeMaitre to Present at the 24th Annual Needham Virtual Healthcare Conference

BURLINGTON, Mass., April 01, 2025 (GLOBE NEWSWIRE) -- LeMaitre Vascular, Inc. (Nasdaq:LMAT) announced today that management will present at the 24th Annual Needham Virtual Healthcare Conference on Tuesday, April 8, 2025, at 3:45 PM EDT. About LeMaitre …

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Published on April 1, 2025 - 15:00 GMT

Cylinder Celebrates 100,000 Members Served, Advancing Access to Digestive Healthcare

CHICAGO, April 01, 2025 (GLOBE NEWSWIRE) -- Cylinder, the leading virtual digestive health provider, today announced a major growth milestone of supporting over 100,000 members across all 50 states. This achievement underscores both the growing demand for …

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Published on April 2, 2025 - 02:07 GMT

House subcommittee holds hearing on cybersecurity vulnerabilities in legacy medical devices

The House Energy and Commerce Oversight and Investigations Subcommittee April 1 discussed cybersecurity threats in legacy medical devices during a hearing. The subcommittee heard from experts on the dangers of outdated devices as the hardware can last …

Distribution channels: Healthcare & Pharmaceuticals Industry

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Published on April 2, 2025 - 01:57 GMT

HALLE BERRY, CVS HEALTH AND TAMSEN FADAL AWARDEES OF WISEPAUSE WELLNESS AT ITS 10TH SUMMIT ON APRIL 12, 2025

WISEPAUSE EMPOWERS WOMEN WITH MENOPAUSE SUPPORT LOS ANGELES, CA, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- WisePause Wellness, the nation’s premier menopause and midlife health event, announces its 10th Summit, taking place on Saturday, …

Distribution channels: Consumer Goods, Culture, Society & Lifestyle ...
Published on April 2, 2025 - 00:22 GMT

Caretaker Medical Receives Inaugural Healthcare Tech Innovation Award and $200,000 Grant from Medical Society of D.C.

WASHINGTON, DC, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- Caretaker Medical is honored to announce it has been awarded the Healthcare Technology Innovation Award, along with a $200,000 grant, from the Medical Society of the District of …

Distribution channels: Banking, Finance & Investment Industry, Emergency Services ...
Published on April 2, 2025 - 00:00 GMT

Startup Care Exhibition Puts Carers and Clients at the Heart of the Conversation

LONDON, KENT, UNITED KINGDOM, April 2, 2025 /⁨EINPresswire.com⁩/ -- Startup Care has announced that its upcoming exhibition will prioritise the voices of carers and private care clients, ensuring their lived experiences are central to the event’s …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on April 1, 2025 - 22:59 GMT

NMAC Condemns Elimination of Federal HIV Programs, Urges Congress and the White House to Reverse Devastating Cuts

WASHINGTON, DC, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- NMAC (formerly the National Minority AIDS Council) strongly condemns the sweeping elimination of key HIV prevention and public health infrastructure at the U.S. Department of …

Distribution channels: Culture, Society & Lifestyle, Healthcare & Pharmaceuticals Industry ...
Published on April 1, 2025 - 22:56 GMT

Açaí Kaa aposta em novas conquistas para 2025 e projeta avanços na COP 30

Reinaldo Santos, CEO da companhia com sede em Belém, prevê lançar açaí em pó para o mercado comercial e o inovador Açaíbot BELEM, PARá, BRAZIL, April 1, 2025 /⁨EINPresswire.com⁩/ -- Reinaldo Santos, CEO da Açaí Kaa, empresa sediada em Belém (PA), projeta …

Distribution channels: Agriculture, Farming & Forestry Industry, Companies ...
Published on April 1, 2025 - 22:47 GMT

Inc. Names Health Advocates Network to Its 2025 List of the Fastest-Growing Private Companies in the Southeast

Companies on the Inc. Regionals: Southeast list had a median growth rate of 114 percent. BOCA RATON, FL, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- Inc., the leading media brand and playbook for the entrepreneurs and business leaders …

Distribution channels: Banking, Finance & Investment Industry, Business & Economy ...
Published on April 1, 2025 - 22:45 GMT

Ketamine Lead Gen Disrupts Wellness Marketing with Proven Lead Generation for TRT and HRT Clinics

Performance marketing agency expands proprietary platform to meet surging demand for hormone optimization services SAN DIEGO, CA, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- As demand for hormone therapy surges nationwide, Ketamine Lead …

Distribution channels: Healthcare & Pharmaceuticals Industry, Media, Advertising & PR ...
Published on April 1, 2025 - 22:28 GMT

Leveling the Field: Riverside Soccer Initiative Supports Local Talent

Focused on equity and access, the Riverside Soccer Initiative funds high school and club athletes through scholarships and travel assistance. RIVERSIDE, CA, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- The Edgar Family Foundation is proud …

Distribution channels: Education, Healthcare & Pharmaceuticals Industry ...
Published on April 1, 2025 - 21:05 GMT

Meeting-Seeking Wildfire Claim to Insurance Company CEO: "I Speak With God Every Day! Why Can't I Speak With You?"

Poignant words from Nurse Pamela Jane Nye after unsuccessful CEO meeting contact attempts to timely resolve Nye's denied Palisades wildfire insurance claim. PACIFIC PALISADES, CA, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- After the Pacific …

Distribution channels: Companies, Healthcare & Pharmaceuticals Industry ...
Published on April 1, 2025 - 20:13 GMT

OCOM Hosts Inaugural Research Symposium to Showcase Student Innovation in Medical Science

OCOM is proud to host its Inaugural Research Symposium on April 4, 2025, celebrating the groundbreaking research and academic excellence of its students. WINTER GARDEN, FL, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- The Orlando College of …

Distribution channels: Education, Healthcare & Pharmaceuticals Industry ...
Published on April 1, 2025 - 19:13 GMT

Tiller-Hewitt Grows List of Clients Across the Country Using Innovative PRM Tool

TrackerPLUS PRM Built By Physician Liaisons For Physician Liaisons ST. LOUIS, MO, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- Four new healthcare organizations have partnered with Tiller-Hewitt HealthCare Strategies to tap into the power …

Distribution channels: Business & Economy, Healthcare & Pharmaceuticals Industry ...
Published on April 1, 2025 - 19:12 GMT

IVF Specialists Now Recommend Single Embryo Transfer for Safer, Healthier Pregnancies

IVF experts now recommend single embryo transfer (SET) for safer pregnancies, reducing risks while maintaining high success rates. NEW YORK, NY, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- Surrogacy4All.com, a leading surrogacy agency and …

Distribution channels: Business & Economy, Healthcare & Pharmaceuticals Industry ...
Published on April 1, 2025 - 18:44 GMT

Donna May Kimmaliardjuk, MD, FRCSC: Shaping the Future of Cardiac Surgery at Cleveland Clinic

Expert in Advanced Cardiac Surgery Techniques Committed to Patient Care and Indigenous Health NEW YORK CITY, NY, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- The Cleveland Clinic is proud to highlight the continued contributions of Donna …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on April 1, 2025 - 18:33 GMT

Scottsdale Detox Recognized as a Top Detox Center in the Southwest, Offering Premier Medical Care and Private Rooms

Scottsdale Detox Recognized as a Top Detox Center in the Southwest, Offering Premier Medical Care and Private Accommodations SCOTTSDALE, AZ, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- Scottsdale Detox Recognized as a Top Detox Center …

Distribution channels: Business & Economy, Education ...
Published on April 1, 2025 - 18:32 GMT

Affordable Patent Services Now Available for Inventors and Startups in Dallas

Affordable Patent Agency offers utility and design patent services for inventors and startups with transparent flat-fee pricing and nationwide access. DALLAS, TX, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- Affordable Patent Agency, LLC …

Distribution channels: Business & Economy, Healthcare & Pharmaceuticals Industry ...
Published on April 1, 2025 - 18:29 GMT

ES Clinical Research Group Supports Clinical Trial Sites and Physicians Nationwide

ES Clinical Research Group supports US clinical trial sites and physicians, providing comprehensive management for Phase I-IV trials. FRESH MEADOWS, NY, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- ES Clinical Research Group, a Site …

Distribution channels: Companies, Education ...
Published on April 1, 2025 - 18:28 GMT

HART Rehab Now In-Network with Blue Cross Blue Shield, Expanding Access to Quality Addiction Treatment Services

HART Rehab Now In-Network with Blue Cross Blue Shield, Expanding Access to Quality Addiction Treatment Services SCOTTSDALE, AZ, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- HART Rehab, a leading provider of comprehensive addiction …

Distribution channels: Business & Economy, Education ...
Published on April 1, 2025 - 17:38 GMT

One-Stop Dental Care Is the Future: Frisco Practices Lead the Way

Patients want simpler care. Elate Orthodontics and Tribute Family Dentistry make it easy by offering multi-specialty dental services in one connected system. FRISCO, TX, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- More and more families …

Distribution channels: Business & Economy, Healthcare & Pharmaceuticals Industry ...
Published on April 1, 2025 - 17:20 GMT

VRIZE Recognized Among the Fastest-Growing Companies in the Inc. Southeast Regionals

VRIZE Secures a Spot in the Southeast’s Top 192, Contributing to 11,493 Jobs and an $8.1B Economic Impact TAMPA, FL, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- Inc. magazine today announced that VRIZE has been ranked No. 43 on its fifth …

Distribution channels: Business & Economy, Food & Beverage Industry ...
Published on April 1, 2025 - 17:07 GMT

New Service Solves Visibility Crisis for Independent Medical Practices

Simple Business Solutions launches turnkey marketing service to help primary care practices stay visible and competitive. REDDING, CA, UNITED STATES, April 1, 2025 /⁨EINPresswire.com⁩/ -- Independent primary care practices across the country are facing a …

Distribution channels: Business & Economy, Healthcare & Pharmaceuticals Industry ...